Question

ITVISMA works by replacing which defective gene associated with spinal muscular atrophy?

A BRCA1 Correct Answer Incorrect Answer
B SMN1 Correct Answer Incorrect Answer
C TP53 Correct Answer Incorrect Answer
D CFTR Correct Answer Incorrect Answer
E MYH7 Correct Answer Incorrect Answer

Solution

As per the report, ITVISMA replaces the defective SMN1 gene, enabling the production of the survival motor neuron protein essential for motor function.

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